TY - JOUR AU - Mannucci, P. M. AU - Tuddenham, E. G. PY - 2001 DA - 2001// TI - The hemophilias--from royal genes to gene therapy JO - N Engl J Med VL - 344 UR - https://doi.org/10.1056/NEJM200106073442307 DO - 10.1056/NEJM200106073442307 ID - Mannucci2001 ER - TY - JOUR AU - Ljung, R. AU - Gretenkort Andersson, N. PY - 2015 DA - 2015// TI - The current status of prophylactic replacement therapy in children and adults with haemophilia JO - Br J Haematol VL - 169 UR - https://doi.org/10.1111/bjh.13365 DO - 10.1111/bjh.13365 ID - Ljung2015 ER - TY - JOUR AU - Ljung, R. C. PY - 2008 DA - 2008// TI - Intracranial haemorrhage in haemophilia a and B JO - Br J Haematol VL - 140 UR - https://doi.org/10.1111/j.1365-2141.2007.06949.x DO - 10.1111/j.1365-2141.2007.06949.x ID - Ljung2008 ER - TY - JOUR AU - White, G. C. AU - Rosendaal, F. AU - Aledort, L. M. AU - Lusher, J. M. AU - Rothschild, C. AU - Ingerslev, J. AU - Factor, V. AU - Factor, I. X. S. PY - 2001 DA - 2001// TI - Definitions in hemophilia. Recommendation of the scientific subcommittee on factor VIII and factor IX of the scientific and standardization committee of the International Society on Thrombosis and Haemostasis JO - Thromb Haemost VL - 85 UR - https://doi.org/10.1055/s-0037-1615621 DO - 10.1055/s-0037-1615621 ID - White2001 ER - TY - JOUR AU - Srivastava, A. AU - Brewer, A. K. AU - Mauser-Bunschoten, E. P. AU - Key, N. S. AU - Kitchen, S. AU - Llinas, A. AU - Ludlam, C. A. AU - Mahlangu, J. N. AU - Mulder, K. AU - Poon, M. C. PY - 2013 DA - 2013// TI - Guidelines for the management of hemophilia JO - Haemophilia VL - 19 UR - https://doi.org/10.1111/j.1365-2516.2012.02909.x DO - 10.1111/j.1365-2516.2012.02909.x ID - Srivastava2013 ER - TY - JOUR AU - Manco-Johnson, M. J. AU - Abshire, T. C. AU - Shapiro, A. D. AU - Riske, B. AU - Hacker, M. R. AU - Kilcoyne, R. AU - Ingram, J. D. AU - Manco-Johnson, M. L. AU - Funk, S. AU - Jacobson, L. PY - 2007 DA - 2007// TI - Prophylaxis versus episodic treatment to prevent joint disease in boys with severe hemophilia JO - N Engl J Med VL - 357 UR - https://doi.org/10.1056/NEJMoa067659 DO - 10.1056/NEJMoa067659 ID - Manco-Johnson2007 ER - TY - JOUR AU - Remor, E. AU - Young, N. L. AU - Mackensen, S. AU - Lopatina, E. G. PY - 2004 DA - 2004// TI - Disease-specific quality-of-life measurement tools for haemophilia patients JO - Haemophilia VL - 10 UR - https://doi.org/10.1111/j.1365-2516.2004.01004.x DO - 10.1111/j.1365-2516.2004.01004.x ID - Remor2004 ER - TY - JOUR AU - Young, N. L. AU - Bradley, C. S. AU - Wakefield, C. D. AU - Barnard, D. AU - Blanchette, V. S. AU - McCusker, P. J. PY - 2006 DA - 2006// TI - How well does the Canadian Haemophilia outcomes-Kids' life assessment tool (CHO-KLAT) measure the quality of life of boys with haemophilia? JO - Pediatr Blood Cancer VL - 47 UR - https://doi.org/10.1002/pbc.20618 DO - 10.1002/pbc.20618 ID - Young2006 ER - TY - JOUR AU - Broderick, C. R. AU - Herbert, R. D. AU - Latimer, J. AU - Curtin, J. A. PY - 2010 DA - 2010// TI - Fitness and quality of life in children with haemophilia JO - Haemophilia VL - 16 UR - https://doi.org/10.1111/j.1365-2516.2009.02096.x DO - 10.1111/j.1365-2516.2009.02096.x ID - Broderick2010 ER - TY - JOUR AU - Net, J. AU - Vos, R. C. AU - Engelbert, R. H. AU - Berg, M. H. AU - Helders, P. J. AU - Takken, T. PY - 2006 DA - 2006// TI - Physical fitness, functional ability and quality of life in children with severe haemophilia: a pilot study JO - Haemophilia VL - 12 UR - https://doi.org/10.1111/j.1365-2516.2006.01307.x DO - 10.1111/j.1365-2516.2006.01307.x ID - Net2006 ER - TY - JOUR AU - St-Louis, J. AU - Urajnik, D. J. AU - Menard, F. AU - Cloutier, S. AU - Klaassen, R. J. AU - Ritchie, B. AU - Rivard, G. E. AU - Warner, M. AU - Blanchette, V. AU - Young, N. L. PY - 2016 DA - 2016// TI - Generic and disease-specific quality of life among youth and young men with hemophilia in Canada JO - BMC Hematol VL - 16 UR - https://doi.org/10.1186/s12878-016-0052-x DO - 10.1186/s12878-016-0052-x ID - St-Louis2016 ER - TY - JOUR AU - Krasuska, M. AU - Riva, S. AU - Fava, L. AU - Mackensen, S. AU - Bullinger, M. PY - 2012 DA - 2012// TI - Linking quality-of-life measures using the international classification of functioning, disability and health and the international classification of functioning, disability and health-children and youth version in chronic health conditions: the example of young people with hemophilia JO - Am J Phys Med Rehabil VL - 91 UR - https://doi.org/10.1097/PHM.0b013e31823d4f35 DO - 10.1097/PHM.0b013e31823d4f35 ID - Krasuska2012 ER - TY - JOUR AU - Taha, M. Y. AU - Hassan, M. K. PY - 2014 DA - 2014// TI - Health-related quality of life in children and adolescents with hemophilia in Basra, southern Iraq JO - J Pediatr Hematol Oncol VL - 36 UR - https://doi.org/10.1097/MPH.0000000000000117 DO - 10.1097/MPH.0000000000000117 ID - Taha2014 ER - TY - JOUR AU - McCusker, P. J. AU - Fischer, K. AU - Holzhauer, S. AU - Meunier, S. AU - Altisent, C. AU - Grainger, J. D. AU - Blanchette, V. S. AU - Burke, T. A. AU - Wakefield, C. AU - Young, N. L. PY - 2015 DA - 2015// TI - International cross-cultural validation study of the Canadian haemophilia outcomes: kids' life assessment tool JO - Haemophilia VL - 21 UR - https://doi.org/10.1111/hae.12597 DO - 10.1111/hae.12597 ID - McCusker2015 ER - TY - JOUR AU - Wu, R. AU - Sun, J. AU - Xiao, J. AU - Liu, Y. AU - Xue, F. AU - Wang, H. AU - Tang, L. AU - Zhao, Y. AU - Li, K. AU - Yang, R. PY - 2017 DA - 2017// TI - A prospective study of health-related quality of life of boys with severe haemophilia a in China: comparing on-demand to prophylaxis treatment JO - Haemophilia VL - 23 UR - https://doi.org/10.1111/hae.13198 DO - 10.1111/hae.13198 ID - Wu2017 ER - TY - JOUR AU - Tang, L. AU - Xu, W. AU - Li, C. G. AU - Hou, F. AU - Feng, X. Q. AU - Wang, H. AU - Li, X. J. AU - Li, W. L. AU - Liu, J. P. AU - Sun, L. R. PY - 2018 DA - 2018// TI - Describing the quality of life of boys with haemophilia in China: results of a multicentre study using the CHO-KLAT JO - Haemophilia VL - 24 UR - https://doi.org/10.1111/hae.13349 DO - 10.1111/hae.13349 ID - Tang2018 ER - TY - JOUR AU - Bradley, C. S. AU - Bullinger, M. AU - McCusker, P. J. AU - Wakefield, C. D. AU - Blanchette, V. S. AU - Young, N. L. PY - 2006 DA - 2006// TI - Comparing two measures of quality of life for children with haemophilia: the CHO-KLAT and the Haemo-QoL JO - Haemophilia VL - 12 UR - https://doi.org/10.1111/j.1365-2516.2006.01346.x DO - 10.1111/j.1365-2516.2006.01346.x ID - Bradley2006 ER - TY - JOUR AU - Young, N. L. AU - Wakefield, C. AU - Burke, T. A. AU - Ray, R. AU - McCusker, P. J. AU - Blanchette, V. PY - 2013 DA - 2013// TI - Updating the Canadian hemophilia outcomes-kids life assessment tool (CHO-KLAT Version2.0) JO - Value Health VL - 16 UR - https://doi.org/10.1016/j.jval.2013.02.004 DO - 10.1016/j.jval.2013.02.004 ID - Young2013 ER - TY - JOUR AU - Wu, R. AU - Zhang, J. AU - Luke, K. H. AU - Wu, X. AU - Burke, T. AU - Tang, L. AU - Poon, M. C. AU - Li, X. AU - Zhou, M. AU - Sun, J. PY - 2012 DA - 2012// TI - Cross-cultural adaptation of the CHO-KLAT for boys with hemophilia in rural and urban China JO - Health Qual Life Outcomes VL - 10 UR - https://doi.org/10.1186/1477-7525-10-112 DO - 10.1186/1477-7525-10-112 ID - Wu2012 ER - TY - JOUR AU - Wu, R. AU - Luke, K. H. PY - 2017 DA - 2017// TI - The benefit of low dose prophylaxis in the treatment of hemophilia: a focus on China JO - Expert Rev Hematol VL - 10 UR - https://doi.org/10.1080/17474086.2017.1386096 DO - 10.1080/17474086.2017.1386096 ID - Wu2017 ER - TY - JOUR AU - Manco-Johnson, M. J. AU - Soucie, J. M. AU - Gill, J. C. PY - 2017 DA - 2017// TI - Joint outcomes Committee of the Universal Data Collection USHTCN: prophylaxis usage, bleeding rates, and joint outcomes of hemophilia, 1999 to 2010: a surveillance project JO - Blood VL - 129 UR - https://doi.org/10.1182/blood-2016-02-683169 DO - 10.1182/blood-2016-02-683169 ID - Manco-Johnson2017 ER - TY - JOUR AU - Ljung, R. PY - 2009 DA - 2009// TI - Prophylactic therapy in haemophilia JO - Blood Rev VL - 23 UR - https://doi.org/10.1016/j.blre.2009.08.001 DO - 10.1016/j.blre.2009.08.001 ID - Ljung2009 ER - TY - JOUR AU - Zilber, R. AU - Bortz, A. P. AU - Yacobovich, J. AU - Yaniv, I. AU - Tamary, H. PY - 2012 DA - 2012// TI - Analysis of health-related quality of life in children with immune thrombocytopenia and their parents using the kids' ITP tools JO - J Pediatr Hematol Oncol VL - 34 UR - https://doi.org/10.1097/MPH.0b013e3182329b4f DO - 10.1097/MPH.0b013e3182329b4f ID - Zilber2012 ER - TY - STD TI - Vepsalainen K, Riikonen P, Lassila R, Arola M, Huttunen P, Lahteenmaki P, Mottonen M, Selander T, Martikainen J. Long-term clinical and economic outcomes in previously untreated paediatric patients with severe haemophilia a: a nationwide real-world study with 700 person-years. Haemophilia. 2018. ID - ref24 ER -